Ionis Pharmaceuticals

the antisense pioneer; the FDA has accepted for Priority Review the New Drug Application for zilganersen in Alexander disease, and Ionis has licensed zilganersen to Recordati for all countries outside the US, extending its Spinraza (nusinersen, SMA) heritage.

Country
United States
Ticker
IONS
Commercial Antisense oligonucleotide
Coverage
CNEUUS
therapeutics-platforms
Regulatorsfdaemanmpa

Verifiable facts

FactValueSource
Capacitynew Oceanside facility more than double the size of existing Carlsbad facilityir.ionis.com
CertificationLEED Silver certification for main Carlsbad headquarters; new research facility designed for LEED Gold certificationionis.com
Regulatory approvalZilganersen granted FDA Breakthrough Therapy, Orphan Drug, Rare Pediatric Disease, and Fast Track designations; NDA accepted for Priority Review with PDUFA date September 22, 2026ir.ionis.com · neurologylive.com
Production siteCarlsbad, California (existing development chemistry and manufacturing facility); Oceanside, California (new manufacturing facility)ionis.com · ir.ionis.com
HeadcountApproximately 1,138 to 1,500 employees medium confidenceionis.com
Revenue$944 million for full year 2025; $267.9 million for first quarter 2026ir.ionis.com · sec.gov

Independent sources: neurologylive.com · sec.gov

Technologies
NameClusterRisk
Nucleic acid therapeutics (oligonucleotides)therapeutics-platformsLow

Compiled by BIOECON from primary sources.

Compliance Bioecon is an information intermediary; it is not a regulator, a certification body, or a legal advisor. When working with public-sector customers (procurement under 44-FZ / 223-FZ), Bioecon acts solely as an independent analytical platform, with no remuneration from suppliers.