Orchard Therapeutics

OTL-200/Libmeldy EMA-approved for MLD; OTL-203 (MPS-I Hurler) completed registrational enrolment 1 year ahead of schedule; OTL-201 (MPS-IIIA) awarded Innovation Passport (UK ILAP) April 2026.

Country
United Kingdom
EMA approved (MLD)
Coverage
CNEUUS
regenerative-personalized
Regulatorsfdaemanmpa
Technologies
NameClusterRisk
Personalized & regenerative medicineregenerative-personalizedMedium

Compiled by BIOECON via the bioecon-brief pipeline.

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