technology
Viral vectors
Engineered viruses (AAV, lentivirus, adenovirus, retrovirus) repurposed as delivery vehicles that transport therapeutic genetic material into target cells for gene therapy and vaccination.
Where it's used
Gene therapy
Precision delivery of functional genetic material via engineered vectors to treat inherited diseases and severe genetic disorders at their root cause.
In-vivo gene therapy: AAV and lentiviral vectors
One-time, potentially curative genetic medicines delivered by engineered adeno-associated and lentiviral vectors — eight FDA-approved in-vivo products since 2017, from Luxturna to Beqvez, now a multi-billion-dollar clinical reality alongside honest commercial retrenchments.